Search Results - gene therapy

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RNA Therapeutics for Diseases Caused by Nonsense Mutations
A method to suppress premature translation termination and NMD to generate full-length protein using target-specific guide RNAs.Problem Solved by the TechnologyA disease-modifying therapy for conditions caused by nonsense mutations, such as Duchenne or Becker muscular dystrophies and cystic fibrosis has long been sought, but to date, none has been ...
Published: 4/10/2014   |   Inventor(s): Yi-Tao Yu, Xinliang Zhao
Keywords(s): Gene, Gene Therapy, Therapy
Category(s): Therapeutic
Freeze-Dried Tendon Allografts as Delivery Vehicles for Genes
Brief Description: This invention is a novel application in tissue engineering and soft tissue (tendon, ligament, skin, cartilage) repair and regeneration. Applications: A large number of therapeutic agents (growth factors and cytokines) have the potential to enhance repair in tendon and ligament allografts. However, our ability to design r...
Published: 4/6/2009   |   Inventor(s): Hani Awad, Edward Schwarz
Keywords(s): Gene, Gene Therapy, Orthopaedics
Category(s): Therapeutic